Retinoic acid and arsenic trioxide trigger degradation of mutated npm1, resulting in apoptosis of aml cells.

The present invention relates to methods and pharmaceutical compositions for the treatment of acute myeloid leukemia. In particular, the present invention relates to a method for treating NPM-1-driven acute myeloid leukemia (AML) in a subject in need thereof comprising administering the subject with a therapeutically effective amount of at least one arsenic compound and with a therapeutically effective amount of at least one retinoid.

Keywords: AML - Combination - Arsenate
Patent Application number: European Procedure (Patents) (EPA) - 30 Déc. 2013 - 13 306 891.6
Inventors:
MARTELLI Maria PaolaFALINI BrunangeloBAZARBACHI AliEL HAJJ Hiba
Publications:
Blood. 2015 May 28;125(22):3447-54. doi: 10.1182/blood-2014-11-612416. Epub 2015 Mar 23.

Reference:

BIO13408-T1

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    Aymeric Empereur
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    Patent filling date: 30-12-2013
    Rare disease: No
    Second indication: Yes

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